1. | kimmycatrat | |
2. | rea3712 | |
3. | ryder69398 | |
4. | honestopete |
1. | kimmycatrat | |
2. | rea3712 | |
3. | ryder69398 | |
4. | honestopete |
1. | rea3712 05/24/2018 BioMarin Receives Standard Approval for Palynziq™ (pegvaliase-pqpz) Injection for Treatment of Adults with Phenylketonuria (PKU), a Rare Genetic Disease |
2. | ryder69398 02/07/2018 Presents interim data from a Phase 1/2 trial for BMN 250 for the treatment of Sanfilippo B syndrome or mucop… |
3. | kimmycatrat 04/24/2018 New England Journal of Medicine Published Open-label Study Showing Brineura® (cerliponase alfa) Reduced the Rate of Clinical Decline of Children with CLN2 Disease, a Form of Batten Disease |
4. | ryder69398 04/30/2018 Morgan Stanley raises PT to $113 from $112 |
5. | kimmycatrat 03/29/2018 Announced the EMA accepted its pegvaliase MAA for the treatment of adults with phenylketonuria who have inad… |