1. kimmycatrat
2. rea3712
3. ryder69398
1.ryder69398 02/07/2018
Presents interim data from a Phase 1/2 trial for BMN 250 for the treatment of Sanfilippo B syndrome or mucop…
2.rea3712 05/24/2018
BioMarin Receives Standard Approval for Palynziq™ (pegvaliase-pqpz) Injection for Treatment of Adults with Phenylketonuria (PKU), a Rare Genetic Disease
3.ryder69398 04/30/2018
Morgan Stanley raises PT to $113 from $112
4.kimmycatrat 03/29/2018
Announced the EMA accepted its pegvaliase MAA for the treatment of adults with phenylketonuria who have inad…
5.kimmycatrat 04/24/2018
New England Journal of Medicine Published Open-label Study Showing Brineura® (cerliponase alfa) Reduced the Rate of Clinical Decline of Children with CLN2 Disease, a Form of Batten Disease
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